New Products

Madrigal Shatters Street Expectations With $62m In Q3 Rezdiffra Sales

Madrigal Shatters Street Expectations With $62m In Q3 Rezdiffra Sales

 
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Doubling some analyst projections for its second full quarter on market, Madrigal’s NASH drug appears headed to blockbuster status and a sustained market position.

Iterum Scores First Approval For Oral Penem Antibiotic

Iterum Scores First Approval For Oral Penem Antibiotic

 

The US FDA approved Orlynvah for uncomplicated urinary tract infections among adult women, despite some concerns about the potential for off-label use and resistance.

Pfizer’s Abrysvo Is First RSV Vaccine Approved For Younger High-Risk Adults

Pfizer’s Abrysvo Is First RSV Vaccine Approved For Younger High-Risk Adults

 

Pfizer beat GSK with a new indication for its RSV vaccine in high-risk individuals aged 18-59.

Astellas Wins Approval For Vyloy, Making Claudin 18.2 Testing Critical

Astellas Wins Approval For Vyloy, Making Claudin 18.2 Testing Critical

 

An exec said the company is confident it can ensure testing for the biomarker becomes routine for the drug, which is the first FDA-approved medicine to target CLDN18.2.


AbbVie Gets Second Parkinson’s Drug With Vyalev Approval

AbbVie Gets Second Parkinson’s Drug With Vyalev Approval

 
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Vyalev, a 24-hour constant infusion of carbidopa and levodopa prodrugs, obtained US FDA approval and will launch at $119,000 per year.

Pfizer’s Hympavzi May Fall Into Hemophilia B Niche

Pfizer’s Hympavzi May Fall Into Hemophilia B Niche

 

The US FDA approved the drug for hemophilia A and B, and while it may struggle to compete in hemophilia A against Roche’s Hemlibra, it has a big convenience advantage in hemophilia B.

Pipeline Watch: Four Approvals And Five Phase III Readouts

Pipeline Watch: Four Approvals And Five Phase III Readouts

 
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Pipeline Watch is a weekly snapshot of selected late-stage clinical trial events and approvals announced by pharmaceutical and biotech companies at medical and industry conferences, in financial and company presentations, and in company releases and statements.

Long-Term Benefits Put PTC Friedreich’s Ataxia Drug Back On Track

Long-Term Benefits Put PTC Friedreich’s Ataxia Drug Back On Track

 
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While vatiquinone may have missed its primary endpoint in a Phase III trial, PTC is ready to file the drug for the debilitating, life-shortening disorder after showing that it slowed disease progression over 144 weeks.


GSK’s Arexvy Reinforces Its Lead In A Stalling RSV Vaccine Market

GSK’s Arexvy Reinforces Its Lead In A Stalling RSV Vaccine Market

 

Arexvy has become the first RSV vaccine to show it can provide protection over three years – but that might mean lower market uptake than originally expected.

Sage NMDA Modulator Fails In Alzheimer’s Months After Parkinson’s Disappointment

Sage NMDA Modulator Fails In Alzheimer’s Months After Parkinson’s Disappointment

 
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Dalzanemdor missed its primary endpoint in a Phase II Parkinson’s study, Sage announced, following April’s Phase II miss in Alzheimer’s. Phase II data in Huntington’s are still expected this year.

Scholar Rock Heading To Finish Line In SMA With Positive Pivotal Data

Scholar Rock Heading To Finish Line In SMA With Positive Pivotal Data

 
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Phase III success positions Scholar Rock’s selective myostatin inhibitor for regulatory filings in early 2025. Analysts see a blockbuster opportunity for additive therapy in spinal muscular atrophy.

Pipeline Watch: Eight Approvals And 11 Phase III Readouts

Pipeline Watch: Eight Approvals And 11 Phase III Readouts

 
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Pipeline Watch is a weekly snapshot of selected late-stage clinical trial events and approvals announced by pharmaceutical and biotech companies at medical and industry conferences, in financial and company presentations, and in company releases and statements.


Bristol’s Opdivo Joins Keytruda, Imfinzi In Perioperative NSCLC Treatment Space

Bristol’s Opdivo Joins Keytruda, Imfinzi In Perioperative NSCLC Treatment Space

 
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PD-1 inhibitor Opdivo has obtained US FDA approval for pre- and post-surgical treatment in operable non-small cell lung cancer, but Merck and AstraZeneca got there first.

Nxera: Building To Become Japan’s Global Biotech Champion

Nxera: Building To Become Japan’s Global Biotech Champion

 

CEO Chris Cargill talks to Scrip about Sosei Heptares’ new identity as Nxera, the ups and downs of being big pharma’s go-to small-molecule drug hunter and its move into commercialization in Japan.

With FDA Hold Lifted, Avidity Works To Bring First DM1 Therapy To Market

With FDA Hold Lifted, Avidity Works To Bring First DM1 Therapy To Market

 
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Avidity hopes to complete enrollment in mid-2025 for an ongoing Phase III trial of its antibody-oligonucleotide conjugate in myotonic dystrophy type 1, which has no approved drug therapy.

Sanofi/Regeneron’s Dupixent:  A First For COPD, But Not The Last

Sanofi/Regeneron’s Dupixent: A First For COPD, But Not The Last

 

The IL-4/13 inhibitor was approved in the US for COPD, a blockbuster-sized indication, but the commercial ramp could take time and several competitors are on its heels. 


Pipeline Watch: 33 Approvals And 19 Phase III Readouts

Pipeline Watch: 33 Approvals And 19 Phase III Readouts

 
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Pipeline Watch is a weekly snapshot of selected late-stage clinical trial events and approvals announced by pharmaceutical and biotech companies at medical and industry conferences, in financial and company presentations, and in company releases and statements.

Enanta’s Phase II Challenge Data Position A Second Potential RSV Therapy

Enanta’s Phase II Challenge Data Position A Second Potential RSV Therapy

 
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One of Enanta’s two antivirals in development for RSV showed efficacy in a healthy patient challenge trial. But analysts say field studies of infected patients are more telling.

BMS To Launch Novel Schizophrenia Therapy Cobenfy Within The Next Month

BMS To Launch Novel Schizophrenia Therapy Cobenfy Within The Next Month

 
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BMS said Cobenfy’s annual list price of $22,500 is in line with other branded antipsychotics and sees the drug as a 2025 launch given late 2024 approval and ongoing reimbursement talks.

AbbVie’s Tavapadon Demonstrates Efficacy In Parkinson’s Monotherapy Study

AbbVie’s Tavapadon Demonstrates Efficacy In Parkinson’s Monotherapy Study

 
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Having earlier shown efficacy as adjunctive therapy, AbbVie is waiting for data from a third Phase III trial before determining filing plans for the D1/D5 receptor agonist.